publication venue for
- A clinically viable approach to restoring visual function using optogenetic gene therapy.. 29. 2023
- Engineering and In Vitro Selection of a Novel AAV3B Variant with High Hepatocyte Tropism and Reduced Seroreactivity.. 19. 2020
- Engineered Antigen-Specific T Cells Secreting Broadly Neutralizing Antibodies: Combining Innate and Adaptive Immune Response against HIV.. 19. 2020
- Analysis of Aflibercept Expression in NHPs following Intravitreal Administration of ADVM-022, a Potential Gene Therapy for nAMD.. 18. 2020
- Experimental Variables that Affect Human Hepatocyte AAV Transduction in Liver Chimeric Mice.. 18. 2020
- HIV-Specific T Cells Can Be Generated against Non-escaped T Cell Epitopes with a GMP-Compliant Manufacturing Platform.. 16. 2019
- Gene Therapy Correction of Aldehyde Dehydrogenase 2 Deficiency.. 15. 2019
- Screening Clinical Cell Products for Replication Competent Retrovirus: The National Gene Vector Biorepository Experience.. 10. 2018
- Dynamics of antigen presentation to transgene product-specific CD4+ T cells and of Treg induction upon hepatic AAV gene transfer.. 3. 2016
- Developmental stage determines efficiency of gene transfer to muscle satellite cells by in utero delivery of adeno-associated virus vector serotype 2/9.. 1. 2014
- Evidence generation and reproducibility in cell and gene therapy research: A call to action.. 22. 2021